Matsui Highlights Needed Progress for Rare Diseases at 21st Century Cures Hearing

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Washington, November 30, 2017 | comments

Washington, D.C. – Today, at a House Energy & Commerce Health Subcommittee hearing on “Implementing the 21st Century Cures Act: An Update from FDA and NIH,” Congresswoman Doris Matsui (D-CA) called for continued progress for the treatment and cures of rare diseases.

“Finding cures for rare diseases is not only important to the patients with rare diseases and their families, but to all of us,” Congresswoman Matsui said. “You never know where a cure is going to come from, and often, research and drug development on one disease may create results for another. So, we need to leverage all the tools that we have.”

Congresswoman Matsui was an architect of provisions in the 21st Century Cures Act that were aimed at encouraging innovation for patients with rare diseases.  This includes sections 3012 through 3016 of the bill, which allow manufacturers to utilize data from previously approved drug applications to seek new indications for rare diseases and which provide incentives for manufacturers to develop drugs in this space. Matsui is a member of the Rare Disease Congressional Caucus, and is committed to continuing to leverage and create policy solutions that accelerate cures.


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